The FDA has accepted PTC Therapeutics' NDA for vatiquinone, a potential treatment for Friedreich's ataxia, with a decision expected by August 19, 2025. PTC Therapeutics has announced that the FDA has ...

Sanjiv Harpavat, MD, PhD, FAAP, lead author of a clinical report recently released by the AAP on identifying infants with biliary atresia, joined to discuss the report and guidance for primary care. A ...

Infant mortality rates increased in US states with abortion bans, reversing previous declines. States with bans saw 478 excess infant deaths, with the highest increases in Texas and Kentucky. Black ...

Managing Comorbidities and Mitigating Atopic March in Adolescent and Adult Patients ...

Real-World Challenges to Providing Evidence-Based Care for Atopic Dermatitis ...

Real-World Challenges to Providing Evidence-Based Care for Atopic Dermatitis ...

Real-World Challenges to Providing Evidence-Based Care for Atopic Dermatitis ...

90-day interim biopsy data in the first 3 patients revealed an average microdystrophin expression of 110% and improvements in muscle health and resilience biomarkers. Positive initial data has been ...

0.05% atropine was associated with a higher incidence of mild side effects, though it was more effective in controlling myopia progression compared to 0.01% atropine or placebo. A new study published ...

In this quiz, we test your knowledge of the AAP's new algorithm and updated recommendations for newborn screening for critical congenital heart disease. In December 2024, the American Academy of ...

Real-World Challenges to Providing Evidence-Based Care for Atopic Dermatitis ...

Panelists discuss the prevalence of treatment-refractory moderate to severe atopic dermatitis, noting factors such as intolerance or inability to use high-potency topical agents as common reasons for ...