Australian researchers have successfully introduced an improved version of Cas12a gene-editing enzyme in mice.
The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...
The UK has approximately 17,500 individuals living with sickle cell disease, a condition particularly prevalent amongst those ...
Design Therapeutics' GeneTAC platform is revolutionizing genetic disease treatment with small molecules and promising results ...
January 31, 2025 expert reaction to NICE final draft guidance on exagamglogene autotemcel (exa-cel) for severe sickle cell disease . Scientists comment on final draft guidance fro ...
NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...
People in England with sickle cell will be able to get the world’s first CRISPR-based medicine under an agreement between the ...
NHS officials estimate that around 50 people a year will receive treatment now that it has been approved for use for certain ...
Britain's National Health Service (NHS) will provide a cutting-edge gene therapy that aims to cure sickle cell disease, the ...
A GROUNDBREAKING genetic treatment with the potential to cure sickle cell disease will be rolled out on the NHS. The one-off ...
A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...